An international study validates the efficacy of a drug in adults with neurofibromatosis type 1
An international study, published in The Lancet, demonstrates for the first time that the drug selumetinib is effective in reducing tumours and associated pain in adults with neurofibromatosis type 1 (NF1). IGTP and Hospital played a key role in the clinical trial, which marks a significant advance in the treatment options for this rare genetic disease.